A Comprehensive Haplotype-Targeting Strategy for Allele-Specific HTT Suppression in Huntington Disease
Chris Kay, Jennifer A. Collins, Nicholas S. Caron, Luciana de Andrade Agostinho, Hailey Findlay-Black, Lorenzo Casal, Dulika Sumathipala, Vajira H.W. Dissanayake, Mario Cornejo-Olivas, Fiona Baine, Amanda Krause, Jacquie L. Greenberg
2019PDF1.2 MB