AAV Mini-dystrophin Gene Therapy for Duchenne Muscular Dystrophy
Russell J. Butterfield & Perry B. Shieh & Huihua Li & Michael Binks & Tara G. McDonnell & Kelly A. Ryan & Marielle Delnomdedieu & Beth A. Belluscio & Srividya Neelakantan & Daniel I. Levy & Pamela F. Schwartz & Edward C. Smith
2025PDF3.7 MB
- EN
