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CLINICAL OUTCOMES OF LENTIGLOBIN GENE THERAPY FOR TRANSFUSION-DEPENDENT β-THALASSAEMIA (TDT) FOLLOWING COMPLETION OF THE NORTHSTAR (HGB-204) STUDY by Walters, M. C.; Kwiatkowski, J. L.; Rasko, J. E.J.; Hongeng, S.; Schiller, G. J.; Anurathapan, U.; Cavazzana, M.; Ho, P. J.; Schmidt, M.; Kletzel, M.; Leboulch, P.; Vichinsky, E.; Deary, B.; Chen, Y.; Petrusich, A.; Thompson, A. A. is a Medicine article available to read on EtoBox.

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Author
Walters, M. C.; Kwiatkowski, J. L.; Rasko, J. E.J.; Hongeng, S.; Schiller, G. J.; Anurathapan, U.; Cavazzana, M.; Ho, P. J.; Schmidt, M.; Kletzel, M.; Leboulch, P.; Vichinsky, E.; Deary, B.; Chen, Y.; Petrusich, A.; Thompson, A. A.
Publisher
Ovid Technologies (Wolters Kluwer) - Lippincott Williams & Wilkins; Ovid Technologies (Wolters Kluwer Health) (ISSN 2572-9241)
Published
2019
Field
Medicine (Health Sciences)

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