About this document
Muscular Dystrophy (Medical Disorder 5) PDF by Benjamine Escaño is a document available to read on EtoBox.
Muscular dystrophy (MD) is a group of genetic disorders leading to progressive muscle degeneration, primarily caused by mutations in the dystrophin gene. Gene therapy aims to correct these genetic defects through methods like gene addition, silencing, and editing, using vectors such as adeno-associated viruses (AAV) to deliver therapeutic genes. Despite challenges in delivery and immune response, advancements in gene therapy offer hope for improving muscle function and quality of life for individuals with M
- Author
- Benjamine Escaño
- Language
- EN