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About this Medicine article
Observational clinical study of 22 adult-onset Pompe disease patients undergoing enzyme replacement therapy over 5years by Stepien, Karolina M.; Hendriksz, Christian J.; Roberts, Mark; Sharma, Reena is a Medicine article available to read on EtoBox.
It is typically read by researchers, students, and practitioners in Medicine.
- Author
- Stepien, Karolina M.; Hendriksz, Christian J.; Roberts, Mark; Sharma, Reena
- Publisher
- Elsevier Science; Elsevier ; Elsevier Inc.; Elsevier BV (ISSN 1096-7192)
- Published
- 2016
- Language
- EN
- Field
- Medicine (Health Sciences)
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