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Lentiviral-Mediated Gene Therapy Results in Sustained Expression of β-Glucuronidase for up to 12 Months in the Gus mps/mps and up to 18 Months in the Gus tm(L175F)Sly Mouse Models of Mucopolysaccharidosis Type VII by Derrick-Roberts, Ainslie L.K.; Pyragius, Carmen E.; Kaidonis, Xenia M.; Jackson, Matilda R.; Anson, Donald S.; Byers, Sharon is a Biochemistry, Genetics and Molecular Biology article available to read on EtoBox.

It is typically read by researchers, students, and practitioners in Biochemistry, Genetics and Molecular Biology.

Author
Derrick-Roberts, Ainslie L.K.; Pyragius, Carmen E.; Kaidonis, Xenia M.; Jackson, Matilda R.; Anson, Donald S.; Byers, Sharon
Publisher
Mary Ann Liebert; Mary Ann Liebert Inc.; Mary Ann Liebert Inc (ISSN 1043-0342)
Published
2014
Language
EN
Field
Biochemistry, Genetics and Molecular Biology (Life Sciences)

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