About this document
Nusinersen for Spinal Muscular Atrophy by Maxwell College is a document available to read on EtoBox.
This systematic review examines the efficacy, safety, and pharmacokinetics of nusinersen treatment in spinal muscular atrophy (SMA) children. The review included 3 studies involving patients with SMA types 1, 2, or 3 who received nusinersen treatment. The studies were conducted in the USA and evaluated outcomes such as motor function scores, survival rates, and adverse events. Nusinersen demonstrated improvements in motor function in SMA patients and an acceptable safety profile.
- Author
- Maxwell College
- Language
- EN